News Story from: Thu, 25 January 2024 | Contains information about a drug called Libmeldy that helps children with a rare and dangerous disease called Metachromatic leukodystrophy (MLD). MLD affects kids’ brains and nervous systems and can be life-threatening. The article also mentions the expensive cost of the drug and negotiations to make it available in Ireland. It discusses the story of a father, Les Martin, who lost his oldest son to MLD but was able to successfully treat his younger son with the drug. Mr. Martin advocates for including MLD in the heel prick test for newborns to detect and treat the disease early.
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– Libmeldy
– Metachromatic leukodystrophy (MLD)
– rare disease
– dangerous disease
– children’s health
– brain disease
– nervous system
– life-threatening
– expensive drug
– negotiations
– Ireland
– loss of a child
– treatment success
– heel prick test
– early detection
– serious disease
– preventing deaths
– legacy
– saving lives
– Libmeldy
– Metachromatic leukodystrophy (MLD)
– rare disease
– dangerous disease
– children’s health
– brain disease
– nervous system
– life-threatening
– expensive drug
– negotiations
– Ireland
– loss of a child
– treatment success
– heel prick test
– early detection
– serious disease
– preventing deaths
– legacy
– saving lives